Lisokabtagen maraleucel
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- Mezinárodní název (INN)
- Lisocabtagenum maraleucelum
- Anglicky
- LISOCABTAGENE MARALEUCEL
Synonyma: HUMAN CULTURE EXPANDED GENETICALLY MODIFIED AUTOLOGOUS T CELLS FOR CELL-BASED GENE THERAPY. CD4+ CD8+ T CELLS ARE DERIVED FROM ISOLATED BLOOD OF THE PATIENT AND ARE TRANSDUCED WITH NON-REPLICATIVE SELF-INACTIVATING (SIM) LENTIVIRAL VECTOR ENCODING AN FMC63 ANTI-CD19 SINGLE CHAIN VARIABLE FRAGMENT (SCFV) LGG4 HINGE REGION/CD28/CD137 (4-1BB)/CD3ZETA CHIMERIC ANTIGEN RECEPTOR (CAR) AND A TRUNCATED FORM OF THE HUMAN EPIDERMAL GROWTH FACTOR RECEPTOR (EGFRT) UNDER THE CONTROL OF THE ELONGATION FACTOR 1-ALPHA (EF1-ALPHA)/R REGION FROM THE HUMAN T CELL LEUKAEMIA VIRUS 1 (HTLV-1 R) COMPOSITE PROMOTER. CELLS EXHIBIT ANTI-TUMORAL ACTIVITY IN PATIENTS WITH CD19-EXPRESSING B CELL MALIGNANCIES · LISOCABTAGEN MARALEUCEL · LISOCABTAGENE MARALEUCEL · LISOCABTAGENUM MARALEUCELUM · LISOKABTAGEN MARALEUCEL
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